Altered retinal vasculature is a biomarker of disease in Spinal Muscular Atrophy in mouse models and human patients

Alison Thomson, Haiyan Zhou, Mariacristina Scoto, Dorothy Thompson, Francesco Catapano, Emma Pead, Tom MacGillivray, Hannah Shorrock, Gillian Hunter, Thomas Gillingwater, Francesco Muntoni, Simon Parson

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